• Scholar Rock Secures U.S. Patent for Potential SMA Therapy Targeting Myostatin
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  • Boston Rare Disease Film Festival to Feature SMA Documentary ‘Life & Atrophy’
  • Machines are Just One Part of Caregiving — 24/7/365
  • One Year Since I Attempted Stand-up Comedy
  • Cure SMA to Host Webinar Today on Spinraza Access
  • Saying No to Shame, Embarrassment and Difficult Physical Activities
  • Life Before and After Spinraza, Part 2
  • Adjusting to Overnight Feeding and More Solid Foods
  • My New Role Here at ‘SMA News Today’
  • Ionis Earns $40 Million Spinraza SMA Regulatory Milestone Payment From Biogen